Substrate Reduction Therapy Sanfilippo A,B,C,D
Medical School, University of Naples Federico II
Dr. Giancarlo Parenti parenti@unina.it
Dr. Paola Di Natale dinatale@dbbm.unina.it

Development of inhibitor of GAG synthesis. Dr. Parenti and Dr. Natale have developed a compound that is an efficient inhibitor of GAG synthesis, thus reducing the amount of heparin sulfate the body produces.