Our Mission
Team Sanfilippo Foundation is led by parents, driven by urgency, and powered by science. We recognize the challenges for children with advanced Sanfilippo Syndrome. We strategically invest in scientific and educational endeavors, as the foundation has been formed to receive and distribute funds for the purposes within the 501(c)(3) of the Internal Revenue Code.
We are a non-profit medical research foundation established in 2008. We support academic centers, biotech, and pharmaceuticals conducting promising research projects intended to slow down or cure the disease.
Team Sanfilippo Foundation has access to treatments and compassionate use options. We look for clinical trial development, push for faster genetic diagnoses, genetic testing, and work hand-in-hand with doctors, scientists, and pharmaceutical companies.
Team Sanfilippo Foundation’s mission is to aid therapies that can be used in clinical trials.
We aim to bring effective therapies to clinical trials by funding research to find a treatment for the disease. We assist in connecting families to companies that need information for ongoing clinical work, actively helping families navigate the clinical trial process. We are committed to ensuring children of all ages can participate in these advancements and support their families.
With exciting progress in enzyme replacement and gene therapy, we are focusing on developing powerful combination therapies. Furthermore, we champion research aimed at understanding and potentially reversing brain damage, especially in synergy with new treatments, to maximize the children’s quality of life. We’re not just hoping for change—we’re building it.
